Clinical Outcome Measures / Clinical Trials of CMT neuropathies
Chair: Maike Dohrn with Alexandre Hoyau
Speaker: Davide Pareyson
Objectives:
• Understand the state of the art and offer new methods including the use of AI for reliable outcome assessment of possible benefits of therapies for iNMDs and CMT in particular
• Harmonization: Perspectives, benefits and risks of standardization of outcome assessment.
Intro talk with discussion 30 min, followed by 5x10 min oral presentations with discussion
Tasks and deliverables:
• Assessment of current methods employed to measure efficacy and benefits of treatments, and approaches
• Identification of conditions for common global standards for clinical outcome measures
• New approaches, including AI, for assessing therapeutic intervention efficacy