Understanding the functional consequences of mutations in the Helsmoortel-Van der Aa and fragile X syndromes

Source
Antwerp, University of Antwerp, Faculty of Pharmaceutical, Biomedical and Veterinary Sciences, Department of Biomedical Sciences,416 p.

A missense variant in the KH0-domain of FMRP downregulates the protein in a patient with the clinical hallmarks of fragile X syndrome

Source
European journal of human genetics - ISSN 1018-4813- (2025) p.
Author(s)