Understanding the functional consequences of mutations in the Helsmoortel-Van der Aa and fragile X syndromes

Source
Antwerp, University of Antwerp, Faculty of Pharmaceutical, Biomedical and Veterinary Sciences, Department of Biomedical Sciences,416 p.

A missense variant in the KH0-domain of FMRP downregulates the protein in a patient with the clinical hallmarks of fragile X syndrome

Source
European journal of human genetics - ISSN 1018-4813- (2025) p.
Author(s)

Whole-genome sequencing reveals individual and cohort level insights into chromosome 9p syndromes

Source
Genome medicine - ISSN 1756-994X-17:1 (2025) p. 1-24
Author(s)
    Yingxi Wang, Eleanor I. Sams, Rachel Slaugh, Sandra Crocker, Emily Cordova Hurtado, Sophia Tracy, Ying-Chen Claire Hou, Christopher Markovic, Kostandin Valle, Victoria Tate, Khadija Belhassan, Elizabeth Appelbaum, Titilope Akinwe, Rodrigo T. Starosta, Yang Cao, Amber Neilson, Yu Liu, Nathaniel Jensen, Reza Ghasemi, Tina Lindsay, Juana Manuel, Sophia Couteranis, Milinn Kremitzki, Jack Ustanik, Thomas Antonacci, Jeffrey K. Ng, Andrew Emory, Laura Metz, Tracie DeLuca, Katherine N. Lyons, Toni Sinnwell, Brianne Thomeczek, Kymme Wang, Nick Sisneros, Megha Muraleedharan, Anantha Kethireddy, Marco Corbo, Harsha Gowda, Katherine A. King, Christina A. Gurnett, Susan K. Dutcher, Catherine Gooch, Yang E. Li, Matthew W. Mitchell, Kevin A. Peterson, Amjad Horani, Jill A. Rosenfeld, Frank Kooy, Dale Annear, Tychele N. Turner