Correlation between patient-derived intestinal organoids and clinical responses to CFTR modulators in people with cystic fibrosis homozygous for F508del

Bron
Journal of cystic fibrosis - ISSN 1569-1993-24:5 (2025) p. 939-945
Auteur(s)
    Noelia Rodriguez Mier, Senne Cuyx, Kris De Boeck, Marijke Proesmans, Mieke Boon, Lieven Dupont, Kaline Arnauts, Elke De Wachter, Stephanie Van Biervliet, Monique Lequesne, Vicky Nowe, Hedwige Boboli, Anabela Santo Ramalho, Francois Vermeulen, Linda Boulanger, Georges Casimir, Benedicte Demeyere, Danny De Looze, Anja Delporte, Isabelle Etienne, Laurence Hanssens, Christiane Knoop, Ann Raman, Dirk Staessen, Eva Van Braeckel, Kim van Hoorenbeeck, Eef Vanderhelst, Stijn Verhulst, Stefanie Vincken