BiP inactivation due to loss of the deAMPylation function of FICD causes a motor neuron disease

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Genetics in medicine - ISSN 1098-3600-24:12 (2022) p. 2487-2500
Auteur(s)
    Adriana P. Rebelo, Ariel Ruiz, Maike F. Dohrn, Melanie Wayand, Amjad Farooq, Matt C. Danzi, Danique Beijer, Brooke Aaron, Jana Vandrovcova, Henry Houlden, Leslie Matalonga, Lisa Abreu, Guy Rouleau, Mehrdad A. Estiar, Liedewei Van de Vondel, Ziv Gan-Or, Jonathan Baets, Rebecca Schüle, Stephan Zuchner

De novo and dominantly inherited SPTAN1 mutations cause spastic paraplegia and cerebellar ataxia

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Movement disorders: video, videotape supplements - ISSN 0885-3185-37:6 (2022) p. 1175-1186
Auteur(s)
    Liedewei Van de Vondel, Jonathan De Winter, Danique Beijer, Giulia Coarelli, Melanie Wayand, Robin Palvadeau, Martje G. Pauly, Katrin Klein, Maren Rautenberg, Léna Guillot‐Noël, Tine Deconinck, Atay Vural, Sibel Ertan, Okan Dogu, Hilmi Uysal, Vesna Brankovic, Rebecca Herzog, Alexis Brice, Alexandra Durr, Stephan Klebe, Friedrich Stock, Almut Turid Bischoff, Tim W. Rattay, María‐Jesús Sobrido, Giovanna De Michele, Peter De Jonghe, Katja Lohmann, Ginevra Zanni, Filippo M. Santorelli, Vincent Timmerman, Tobias B. Haack, Stephan Züchner, Rebecca Schüle, Giovanni Stevanin, Matthis Synofzik, A. Nazli Basak, Jonathan Baets

Solve-RD : systematic pan-European data sharing and collaborative analysis to solve rare diseases

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European journal of human genetics - ISSN 1018-4813-29:9 (2021) p. 1325-1331
Auteur(s)
    Birte Zurek, Kornelia Ellwanger, Lisenka E.L.M. Vissers, Rebecca Schuele, Matthis Synofzik, Ana Topf, Richarda M. de Voer, Steven Laurie, Leslie Matalonga, Christian Gilissen, Stephan Ossowski, Peter A.C. 't Hoen, Antonio Vitobello, Julia M. Schulze-Hentrich, Olaf Riess, Han G. Brunner, Anthony J. Brookes, Ana Rath, Gisele Bonne, Gulcin Gumus, Alain Verloes, Nicoline Hoogerbrugge, Teresinha Evangelista, Tina Harmuth, Morris Swertz, Dylan Spalding, Alexander Hoischen, Sergi Beltran, Holm Graessner, Vincent Timmerman, Liedewei Van de Vondel, Danique Beijer, Peter De Jonghe, Jonathan Baets, Solve-RD consortium